Who We Are
Driven by our proprietary Enhanced Delivery Oligonucleotide (EDO) platform, we are creating a pipeline of disease-modifying therapeutics with the potential to safely and effectively target the root cause of serious genetic neuromuscular and neurological disorders.
Learn More-
Our Pipeline
Advancing transformative therapies to treat neuromuscular and neurological disorders
Learn More -
Our Community
Committed to changing the lives of people living with neuromuscular and neurological disorders
Learn More